N1C Gene Registry

N-of-1 Projects

Explore available and ongoing N-of-1 and N-of-few therapy developments.

Marketed Genetic Therapies

Browse currently approved and marketed genetic therapies.

Assessed Variants

View curated assessments of variants and their therapeutic eligibility.

Published Genetic Therapies

Genetic therapies reported in the scientific literature.

Coming soon.

Assessed Genes & Diseases

Browse genes and diseases that have been assessed for potential genetic therapeutic strategies.

Coming soon.

Automated Assessment Tools

Explore tools that automate the eligibility assessments.

Coming soon.

News

The N1C Gene Registry's data is now also available on DECIPHER. You can find the N-of-1 projects, the marketed drugs as well as the assessed variants on the respective gene and variant pages. (2026 - 06 - 11)

Info

Looking to integrate or access our data? Contact us for access to our API.