Are you developing a therapeutic approach for a specific genetic variant? Share your work with the N1C Gene Registry to increase visibility and collaboration. Submit your project below or follow this LINK for bulk entry. Please reach out to generegistry@n1collaborative.org for any questions related to the Gene Registry.
Submit Your Project
Clinical Application:Clinical Application: The therapy has been fully developed and has been administered to at least one patient globally.
Developed: The therapy has been pre-clinically developed but has not yet been clinically implemented.
Under Development:The therapy is currently under development. This can be at different stages of the development, e.g., very early phases during which compounds are screened pre-clinically, animal testing, or at the manufacturing stage. For more information on the progress of one of the projects under development, please reach out to the respective contact person.
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n-Lorem Portfolio: n-Lorem is an independent non-profit organisation developing antisense oligonucleotides. For more information on their ASOs, please reach out to n-Lorem directly: https://www.nlorem.org/patients/active-gene-programs/
Looking to integrate or access our data? Visit the N1C API documentation.